Gene Therapy: The Power of Advocacy \u0026 Real World Evidence -- PPMD 2023 Annual Conference

(54:57)

Webinar: SRP-9001 Micro-Dystrophin Gene Therapy Clinical Update (October 2021)

(1:9:52)

In the Pipeline: Gene Therapy - Sarepta Therapeutics

(18:41)

Webinar: SRP-9001 Micro-Dystrophin Gene Therapy Clinical Update (June 2021)

(1:5:59)

DMD Gene Therapy Clinical Trials

(5:9)

Duchenne Muscular Dystrophy and Dystrophin

(8:23)

Gene Therapy for DMD How it Works and the Ongoing Clinical Trials

(48:57)

Introduction to Gene Therapy [PPMD Gene Therapy Webinar Series]

(17:28)

Scientists restore muscle strength in dogs using micro-dystrophin gene therapy

(2:46)

Microdystrophin Gene Therapy for Musculoskeletal Diseases | Palani Palaniappan, Ph.D.

(24:18)

DMD and Gene Therapy What's On the Horizon

(32:39)

PPMD 2018 Conference - Restoring or Replacing Dystrophin

(2:4:41)

Webinar: Dystrophin Quantification in Preclinical and Clinical Settings

(52:47)

A film about some of the challenges in gene therapy, and a promising new approach

(5:47)

First Approved Gene Therapy for Muscular Dystrophy Brings Hope to Kids Everywhere

(1:56)

Gene editing for muscular dystrophies

(25:42)

ELEVIDYS and Genetic Variants

(4:3)

022 - Sarepta Declines on Good Micro-Dystrophin Data

(25:20)

Sarepta Announces FDA Approval of ELEVIDYS

(20:56)

MDA Engage: Gene Therapy and Duchenne Muscular Dystrophy

(1:33)